van der Sluijs, Pleuntje J., Jansen, Sandra, Vergano, Samantha A., Adachi-Fukuda, Miho, Alanay, Yasemin ORCID: 0000-0003-0683-9731, AlKindy, Adila, Baban, Anwar, Bayat, Allan, Beck-Woedl, Stefanie, Berry, Katherine, Bijlsma, Emilia K., Bok, Levinus A., Brouwer, Alwin F. J., van der Burgt, Ineke, Campeau, Philippe M., Canham, Natalie, Chrzanowska, Krystyna ORCID: 0000-0003-3888-0624, Chu, Yoyo W. Y., Chung, Brain H. Y., Dahan, Karin, De Rademaeker, Marjan, Destree, Anne, Dudding-Byth, Tracy, Earl, Rachel, Elcioglu, Nursel, Elias, Ellen R., Fagerberg, Christina, Gardham, Alice, Gener, Blanca, Gerkes, Erica H., Grasshoff, Ute, van Haeringen, Arie, Heitink, Karin R., Herkert, Johanna C., den Hollander, Nicolette S., Horn, Denise, Hunt, David, Kant, Sarina G., Kato, Mitsuhiro, Kayserili, Hulya, Kersseboom, Rogier, Kilic, Esra, Krajewska-Walasek, Malgorzata ORCID: 0000-0001-8721-210X, Lammers, Kylin, Laulund, Lone W., Lederer, Damien, Lees, Melissa, Lopez-Gonzalez, Vanesa, Maas, Saskia, Mancini, Grazia M. S., Marcelis, Carlo, Martinez, Francisco ORCID: 0000-0002-0589-2584, Maystadt, Isabelle, McGuire, Marianne, McKee, Shane ORCID: 0000-0002-1772-0106, Mehta, Sarju, Metcalfe, Kay, Milunsky, Jeff, Mizuno, Seiji, Moeschler, John B., Netzer, Christian, Ockeloen, Charlotte W., Oehl-Jaschkowitz, Barbara, Okamoto, Nobuhiko, Olminkhof, Sharon N. M., Orellana, Carmen ORCID: 0000-0003-4271-5859, Pasquier, Laurent ORCID: 0000-0003-3985-1286, Pottinger, Caroline, Riehmer, Vera, Robertson, Stephen P., Roifman, Maian, Rooryck, Caroline ORCID: 0000-0002-9789-3591, Ropers, Fabienne G., Rosello, Monica ORCID: 0000-0001-9234-2953, Ruivenkamp, Claudia A. L., Sagiroglu, Mahmut S., Sallevelt, Suzanne C. E. H., Sanchis Calvo, Amparo, Simsek-Kiper, Pelin O., Soares, Gabriela, Solaeche, Lucia, Sonmez, Fatma Mujgan, Splitt, Miranda, Steenbeek, Duco, Stegmann, Alexander P. A., Stumpel, Constance T. R. M., Tanabe, Saori, Uctepe, Eyyup, Utine, G. Eda, Veenstra-Knol, Hermine E., Venkateswaran, Sunita, Vilain, Catheline, Vincent-Delorme, Catherine, Vulto-van Silfhout, Anneke T., Wheeler, Patricia, Wilson, Golder N., Wilson, Louise C., Wollnik, Bernd, Kosho, Tomoki, Wieczorek, Dagmar, Eichler, Evan, Pfundt, Rolph, de Vries, Bert B. A., Clayton-Smith, Jill and Santen, Gijs W. E.
(2019).
The ARID1B spectrum in 143 patients: from nonsyndromic intellectual disability to Coffin-Siris syndrome.
Genet. Med., 21 (6).
S. 1295 - 1308.
NEW YORK:
NATURE PUBLISHING GROUP.
ISSN 1530-0366
Full text not available from this repository.
Abstract
Purpose: Pathogenic variants in ARID1B are one of the most frequent causes of intellectual disability (ID) as determined by large-scale exome sequencing studies. Most studies published thus far describe clinically diagnosed Coffin-Siris patients (ARID1BCSS) and it is unclear whether these data are representative for patients identified through sequencing of unbiased ID cohorts (ARID1B-ID). We therefore sought to determine genotypic and phenotypic differences between ARID1B-ID and ARID1B-CSS. In parallel, we investigated the effect of different methods of phenotype reporting. Methods: Clinicians entered clinical data in an extensive webbased survey. Results: 79 ARID1B-CSS and 64 ARID1B-ID patients were included. CSS-associated dysmorphic features, such as thick eyebrows, long eyelashes, thick alae nasi, long and/or broad philtrum, small nails and small or absent fifth distal phalanx and hypertrichosis, were observed significantly more often (p < 0.001) in ARID1B-CSS patients. No other significant differences were identified. Conclusion: There are only minor differences between ARID1BID and ARID1B-CSS patients. ARID1B-related disorders seem to consist of a spectrum, and patients should be managed similarly. We demonstrated that data collection methods without an explicit option to report the absence of a feature (such as most Human Phenotype Ontology-based methods) tended to underestimate gene-related features.
Item Type: |
Journal Article
|
Creators: |
Creators | Email | ORCID | ORCID Put Code |
---|
van der Sluijs, Pleuntje J. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Jansen, Sandra | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Vergano, Samantha A. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Adachi-Fukuda, Miho | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Alanay, Yasemin | UNSPECIFIED | orcid.org/0000-0003-0683-9731 | UNSPECIFIED | AlKindy, Adila | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Baban, Anwar | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Bayat, Allan | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Beck-Woedl, Stefanie | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Berry, Katherine | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Bijlsma, Emilia K. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Bok, Levinus A. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Brouwer, Alwin F. J. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | van der Burgt, Ineke | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Campeau, Philippe M. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Canham, Natalie | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Chrzanowska, Krystyna | UNSPECIFIED | orcid.org/0000-0003-3888-0624 | UNSPECIFIED | Chu, Yoyo W. Y. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Chung, Brain H. Y. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Dahan, Karin | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | De Rademaeker, Marjan | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Destree, Anne | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Dudding-Byth, Tracy | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Earl, Rachel | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Elcioglu, Nursel | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Elias, Ellen R. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Fagerberg, Christina | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Gardham, Alice | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Gener, Blanca | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Gerkes, Erica H. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Grasshoff, Ute | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | van Haeringen, Arie | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Heitink, Karin R. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Herkert, Johanna C. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | den Hollander, Nicolette S. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Horn, Denise | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Hunt, David | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Kant, Sarina G. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Kato, Mitsuhiro | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Kayserili, Hulya | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Kersseboom, Rogier | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Kilic, Esra | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Krajewska-Walasek, Malgorzata | UNSPECIFIED | orcid.org/0000-0001-8721-210X | UNSPECIFIED | Lammers, Kylin | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Laulund, Lone W. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Lederer, Damien | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Lees, Melissa | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Lopez-Gonzalez, Vanesa | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Maas, Saskia | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Mancini, Grazia M. S. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Marcelis, Carlo | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Martinez, Francisco | UNSPECIFIED | orcid.org/0000-0002-0589-2584 | UNSPECIFIED | Maystadt, Isabelle | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | McGuire, Marianne | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | McKee, Shane | UNSPECIFIED | orcid.org/0000-0002-1772-0106 | UNSPECIFIED | Mehta, Sarju | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Metcalfe, Kay | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Milunsky, Jeff | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Mizuno, Seiji | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Moeschler, John B. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Netzer, Christian | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Ockeloen, Charlotte W. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Oehl-Jaschkowitz, Barbara | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Okamoto, Nobuhiko | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Olminkhof, Sharon N. M. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Orellana, Carmen | UNSPECIFIED | orcid.org/0000-0003-4271-5859 | UNSPECIFIED | Pasquier, Laurent | UNSPECIFIED | orcid.org/0000-0003-3985-1286 | UNSPECIFIED | Pottinger, Caroline | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Riehmer, Vera | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Robertson, Stephen P. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Roifman, Maian | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Rooryck, Caroline | UNSPECIFIED | orcid.org/0000-0002-9789-3591 | UNSPECIFIED | Ropers, Fabienne G. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Rosello, Monica | UNSPECIFIED | orcid.org/0000-0001-9234-2953 | UNSPECIFIED | Ruivenkamp, Claudia A. L. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Sagiroglu, Mahmut S. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Sallevelt, Suzanne C. E. H. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Sanchis Calvo, Amparo | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Simsek-Kiper, Pelin O. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Soares, Gabriela | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Solaeche, Lucia | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Sonmez, Fatma Mujgan | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Splitt, Miranda | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Steenbeek, Duco | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Stegmann, Alexander P. A. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Stumpel, Constance T. R. M. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Tanabe, Saori | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Uctepe, Eyyup | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Utine, G. Eda | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Veenstra-Knol, Hermine E. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Venkateswaran, Sunita | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Vilain, Catheline | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Vincent-Delorme, Catherine | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Vulto-van Silfhout, Anneke T. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Wheeler, Patricia | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Wilson, Golder N. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Wilson, Louise C. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Wollnik, Bernd | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Kosho, Tomoki | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Wieczorek, Dagmar | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Eichler, Evan | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Pfundt, Rolph | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | de Vries, Bert B. A. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Clayton-Smith, Jill | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED | Santen, Gijs W. E. | UNSPECIFIED | UNSPECIFIED | UNSPECIFIED |
|
URN: |
urn:nbn:de:hbz:38-146787 |
DOI: |
10.1038/s41436-018-0330-z |
Journal or Publication Title: |
Genet. Med. |
Volume: |
21 |
Number: |
6 |
Page Range: |
S. 1295 - 1308 |
Date: |
2019 |
Publisher: |
NATURE PUBLISHING GROUP |
Place of Publication: |
NEW YORK |
ISSN: |
1530-0366 |
Language: |
English |
Faculty: |
Unspecified |
Divisions: |
Unspecified |
Subjects: |
no entry |
Uncontrolled Keywords: |
Keywords | Language |
---|
CHROMATIN-REMODELING COMPLEX; MUTATIONS; PHENOTYPE | Multiple languages | Genetics & Heredity | Multiple languages |
|
Refereed: |
Yes |
URI: |
http://kups.ub.uni-koeln.de/id/eprint/14678 |
Downloads per month over past year
Export