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2020
Lenders, Malte, Nordbeck, Peter ORCID: 0000-0002-2560-4068, Kurschat, Christine, Karabul, Nesrin, Kaufeld, Jessica, Hennermann, Julia B., Patten, Monica, Cybulla, Markus, Muentze, Jonas, Ueceyler, Nurcan, Liu, Dan, Das, Anibh M., Sommer, Claudia, Pogoda, Christian, Reiermann, Stefanie, Duning, Thomas, Gaedeke, Jens, Stumpfe, Katharina, Blaschke, Daniela, Brand, Stefan-Martin, Mann, W. Alexander, Kampmann, Christoph, Muschol, Nicole, Canaan-Kuehl, Sima and Brand, Eva (2020). Treatment of Fabry's Disease With Migalastat: Outcome From a Prospective Observational Multicenter Study (FAMOUS). Clin. Pharmacol. Ther., 108 (2). S. 326 - 338. HOBOKEN: WILEY. ISSN 1532-6535
Voelker, Linus A., Kaufeld, Jessica, Miesbach, Wolfgang, Braehler, Sebastian, Reinhardt, Martin ORCID: 0000-0002-7862-0993, Kuehne, Lucas, Muehlfeld, Anja, Schreiber, Adrian, Gaedeke, Jens, Toelle, Markus, Jabs, Wolfram J., Oezcan, Fedai, Markau, Silke, Girndt, Matthias ORCID: 0000-0003-2823-0847, Bauer, Frederic, Westhoff, Timm H., Felten, Helmut, Hausberg, Martin, Brand, Marcus, Gerth, Jens, Bieringer, Markus, Bommer, Martin, Zschiedrich, Stefan, Schneider, Johanna, Elitok, Saban, Gawlik, Alexander, Gaeckler, Anja, Kribben, Andreas, Schwenger, Vedat, Schoenermarck, Ulf, Roeder, Maximilian, Radermacher, Joerg, Bramstedt, Joern, Morgner, Anke, Herbst, Regina, Harth, Ana, Potthoff, Sebastian A., von Auer, Charis, Wendt, Ralph, Christ, Hildegard ORCID: 0000-0003-3235-2994, Brinkkoetter, Paul T. and Menne, Jan (2020). Real-world data confirm the effectiveness of caplacizumab in acquired thrombotic thrombocytopenic purpura. Blood Adv., 4 (13). S. 3085 - 3093. WASHINGTON: AMER SOC HEMATOLOGY. ISSN 2473-9537
Voelker, Linus A., Kaufeld, Jessica, Miesbach, Wolfgang, Braehler, Sebastian, Reinhardt, Martin ORCID: 0000-0002-7862-0993, Kuehne, Lucas, Muehlfeld, Anja, Schreiber, Adrian, Gaedeke, Jens, Toelle, Markus, Jabs, Wolfram J., Ozcan, Fedai, Markau, Silke, Girndt, Matthias ORCID: 0000-0003-2823-0847, Bauer, Frederic, Westhoff, Timm H., Felten, Helmut, Hausberg, Martin, Brand, Marcus, Gerth, Jens, Bieringer, Markus, Bommer, Martin, Zschiedrich, Stefan, Schneider, Johanna, Elitok, Saban, Gawlik, Alexander, Gaeckler, Anja, Kribben, Andreas, Schwenger, Vedat, Schoenermarck, Ulf, Roeder, Maximilian, Radermacher, Joerg, Bramstedt, Joern, Morgner, Anke, Herbst, Regina, Harth, Ana, Potthoff, Sebastian A., von Auer, Charis, Wendt, Ralph, Christ, Hildegard ORCID: 0000-0003-3235-2994, Brinkkoetter, Paul T. and Menne, Jan (2020). ADAMTS13 and VWF activities guide individualized caplacizumab treatment in patients with aTTP. Blood Adv., 4 (13). S. 3093 - 3102. WASHINGTON: AMER SOC HEMATOLOGY. ISSN 2473-9537