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2020
Lenders, Malte, Nordbeck, Peter ORCID: 0000-0002-2560-4068, Kurschat, Christine, Karabul, Nesrin, Kaufeld, Jessica, Hennermann, Julia B., Patten, Monica, Cybulla, Markus, Muentze, Jonas, Ueceyler, Nurcan, Liu, Dan, Das, Anibh M., Sommer, Claudia, Pogoda, Christian, Reiermann, Stefanie, Duning, Thomas, Gaedeke, Jens, Stumpfe, Katharina, Blaschke, Daniela, Brand, Stefan-Martin, Mann, W. Alexander, Kampmann, Christoph, Muschol, Nicole, Canaan-Kuehl, Sima and Brand, Eva
(2020).
Treatment of Fabry's Disease With Migalastat: Outcome From a Prospective Observational Multicenter Study (FAMOUS).
Clin. Pharmacol. Ther., 108 (2).
S. 326 - 338.
HOBOKEN:
WILEY.
ISSN 1532-6535
2018
Pohl, Sandra, Angermann, Alexandra, Jeschke, Anke, Hendrickx, Gretl ORCID: 0000-0001-6715-9241, Yorgan, Timur A., Makrypidi-Fraune, Georgia, Steigert, Anita, Kuehn, Sonja C., Rolvien, Tim, Schweizer, Michaela, Koehne, Till, Neven, Mona, Winter, Olga, Velho, Renata Voltolini, Albers, Joachim, Streichert, Thomas, Pestka, Jan M., Baldauf, Christina, Breyer, Sandra, Stuecker, Ralf, Muschol, Nicole, Cox, Timothy M., Saftig, Paul, Paganini, Chiara, Rossi, Antonio, Amling, Michael, Braulke, Thomas
ORCID: 0000-0002-2336-8532 and Schinke, Thorsten
(2018).
The Lysosomal Protein Arylsulfatase B Is a Key Enzyme Involved in Skeletal Turnover.
J. Bone Miner. Res., 33 (12).
S. 2186 - 2202.
HOBOKEN:
WILEY.
ISSN 1523-4681