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Lenders, Malte ORCID: 0000-0001-8409-2886, Nordbeck, Peter ORCID: 0000-0002-2560-4068, Kurschat, Christine, Eveslage, Maria ORCID: 0000-0002-8802-1134, Karabul, Nesrin, Kaufeld, Jessica, Hennermann, Julia B., Patten, Monica, Cybulla, Markus, Muentze, Jonas, Ueceyler, Nurcan, Liu, Dan, Das, Anibh M., Sommer, Claudia, Pogoda, Christian, Reiermann, Stefanie, Duning, Thomas, Gaedeke, Jens, Stumpfe, Katharina, Blaschke, Daniela, Brand, Stefan-Martin, Mann, W. Alexander, Kampmann, Christoph, Muschol, Nicole, Canaan-Kuhl, Sima and Brand, Eva . Treatment of Fabry Disease management with migalastat-outcome from a prospective 24 months observational multicenter study (FAMOUS). EUR. HEART J.-CARDIOVASC. PHARMACOTHER.. OXFORD: OXFORD UNIV PRESS. ISSN 2055-6845
Lenders, Malte, Nordbeck, Peter ORCID: 0000-0002-2560-4068, Kurschat, Christine, Karabul, Nesrin, Kaufeld, Jessica, Hennermann, Julia B., Patten, Monica, Cybulla, Markus, Muentze, Jonas, Ueceyler, Nurcan, Liu, Dan, Das, Anibh M., Sommer, Claudia, Pogoda, Christian, Reiermann, Stefanie, Duning, Thomas, Gaedeke, Jens, Stumpfe, Katharina, Blaschke, Daniela, Brand, Stefan-Martin, Mann, W. Alexander, Kampmann, Christoph, Muschol, Nicole, Canaan-Kuehl, Sima and Brand, Eva (2020). Treatment of Fabry's Disease With Migalastat: Outcome From a Prospective Observational Multicenter Study (FAMOUS). Clin. Pharmacol. Ther., 108 (2). S. 326 - 338. HOBOKEN: WILEY. ISSN 1532-6535
Pohl, Sandra, Angermann, Alexandra, Jeschke, Anke, Hendrickx, Gretl ORCID: 0000-0001-6715-9241, Yorgan, Timur A., Makrypidi-Fraune, Georgia, Steigert, Anita, Kuehn, Sonja C., Rolvien, Tim, Schweizer, Michaela, Koehne, Till, Neven, Mona, Winter, Olga, Velho, Renata Voltolini, Albers, Joachim, Streichert, Thomas, Pestka, Jan M., Baldauf, Christina, Breyer, Sandra, Stuecker, Ralf, Muschol, Nicole, Cox, Timothy M., Saftig, Paul, Paganini, Chiara, Rossi, Antonio, Amling, Michael, Braulke, Thomas ORCID: 0000-0002-2336-8532 and Schinke, Thorsten (2018). The Lysosomal Protein Arylsulfatase B Is a Key Enzyme Involved in Skeletal Turnover. J. Bone Miner. Res., 33 (12). S. 2186 - 2202. HOBOKEN: WILEY. ISSN 1523-4681